A translational framework for early-phase inner-ear gene therapy: clinical trial design, regulatory strategy, and ethical considerations.
The genetics of hearing loss is transitioning from a diagnostic modality to an interventional one, with emphasis on emerging gene-based therapies, clinical trial design, regulatory and ethical considerations, and practical implications for otolaryngologists as biologic treatment enters clinical practice.
Emma C. Dunn, Spencer H Short, Ravi N Samy
· Current Opinion in Otolaryng... · 0 citations