Olli-Petteri Nivaro

Moniemäksinen geeniterapia lentiviraalisesti toimitetuilla Cas9(D10A):lla ja HDR-tehostajilla

The accumulation of mutations is the primary generator of hereditary diseases as well as ostensibly much of the symptomatology of aging. Various methods for the therapeutic repair of mutations have been devised, but most have focused on the repair of known hereditary diseases of fixed location, with none having demonst...