The expanding therapeutic landscape of β-thalassaemia.
β-thalassaemia is characterised by ineffective erythropoiesis, chronic anaemia, haemolysis, and progressive iron-related and non-iron-related morbidity. Although transfusion, iron chelation, multidisciplinary care, and allogeneic haematopoietic stem-cell transplantation have substantially improved outcomes, major gaps...
K. Musallam, Sujit Sheth, Franco Locatelli et al.
· The Lancet Haematology · 1 citation