Parthenolide boosts megakaryocyte maturation and restores platelet responses in Wiskott–Aldrich syndrome
Wiskott-Aldrich syndrome (WAS) is an inborn error of immunity with a broad disease spectrum, classified into class I (late onset) or II (early onset) variants. Thrombocytopenia and small platelets are the most consistent findings among patients, difficult to treat and related to development of autoimmunity. To identify...
R. Vieira, Lia Goncalves Pinho, Tracer Yong et al.
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