Unlocking the Curative Potential of Gene Transfer and Editing for Hematopoietic Disorders.
Recent developments and refinements in gene transfer and editing technologies for HSPCs are reviewed, while also discussing the critical limitations and hurdles to clinical translation, as recently presented at the New Investigator Committee Gene Therapy webinar.
Kohei Shiroshita, A. Stolz, C. Malouf et al.
· Experimental Hematology · 0 citations