pH-dependent anti-TfR1 NANOBODY® molecules deliver efficacious oligonucleotide payloads to muscle and CNS tissues
EA Hoyt
K. Moonens
C. Rapisarda
AM Salvador
TR Hammond
S. Kharade
R. Mondragon-Gonzalez
F. Moran
S. Ramkumar
J. Thummapudi
S. Zhou
G. Haussy
C. Capdevila
F. Maillard
A. Ismail
L. Avery
P. Sardi
C. Nonne
S. Cornelis
N. Leksa
Biology