Open access
Pharmacological BET Protein Inhibition Reverts Niemann-Pick Type C Disease-Associated Changes in Human iPSC-Derived Cortical Neurons
F. Benigni
M. Parente
C. Marioli
R. Borghi
N. Cicolani
A. Barthelemy
S. Petrini
M. Tartaglia
FW. Pfrieger
V. Pallottini
C. Compagnucci
Biology