Targeting trafficking defects in long QT syndrome type 2: a phase 2 clinical study with patient-specific cellular validation.
L. Crotti
Federica Dagradi
M. Mura
Fulvio L. F. Giovenzana
Miriam G. Lorusso
Paolo Cerea
C. Alberio
Prabin Upadhyaya
A. Di Mise
M. Pedrazzini
C. Spazzolini
L. Sala
Giulia Musu
M. Gnecchi
Peter J. Schwartz
Medicine