Metabolomic profiling in treated mucopolysaccharidosis IH reveals candidate biomarkers and adjunctive therapeutic pathways
T. Lund
R. Peretz
P. I. Dickson
J.-K. Yee
M. Iacovino
K. Taylor
D. Elashoff
E. Fung
B. Miller
P. Orchard
L. Polgreen
Medicine