Review
Open access
Sep 2026
Biotechnological and Cellular Therapies in the Treatment of Neurodegenerative Leukodystrophies
Leukodystrophies are inherited neurodegenerative disorders characterized by progressive white matter damage, historically lacking effective treatments beyond symptomatic management and hematopoietic stem cell transplantation. This review analyzes contemporary biotechnological strategies, including gene therapy, cell-ba...
A. I. Ayupova, Tatiana S. Tsaregorodtseva, V. Solovyeva et al.
· Personalized Psychiatry and... · 0 citations