Open access
Sep 2026
Fenfluramine in Rett syndrome: A multidimensional clinical study
Fenfluramine was associated with clinically meaningful improvements across several symptom domains in patients with RTT, including seizures, respiratory dysfunction, behavior, sleep, and overall disease severity, with an acceptable safety profile.
E. González-Alguacil, Nuria Lamagrande Casanova, Manuel Luján-Bonete et al.
· Epilepsia Open · 0 citations