Review
Open access
Aug 2026
Targeted Therapy for Restoring CFTR Activity: From Experimental to Clinical Features
The focus of this review is to describe and discuss the strategies for restoring the CFTR functional defects depending on the specific CFTR pathogenic variants, and the possible application of experimental and clinical drugs to CF treatment, which may allow improvements in patients’ quality of life and life expectancy.
Sara Allushi, M. Virgulti, Giovanna Blaconà et al.
· International Journal of Mol... · 0 citations