Open access
Jul 2026
Implementing a First-in-Human Clinical Trial of Prime-Editing Gene Therapy in p47-CGD: Clinical Data and Site Perspectives
While the patient’s clinical course was simple, setting up the clinical trial required acrobatics and coordination worthy of a hyperactive octopus, implementing a first-in-human therapy for patients whose lives are not immediately at risk represents a high degree of complexity.
K. Leveillé, J. Gori, S. Turvey et al.
· Journal of Human Immunity · 0 citations