Open access
Jul 2026
Restoring Parkin Function: An AAV Gene Therapy Approach for Early-Onset Parkinson’s Disease
The results support the potential of AAV-Parkin gene therapy as a disease-modifying approach for Parkin-deficient EOPD and developed a translatable gene therapy approach using rodents.
S. Basu, Tyler G. Demarest, Nicholas J. Gattone et al.
· bioRxiv · 0 citations