Open access
Aug 2026
Long-read target enrichment sequencing for rAAV integration site analysis in engineered clones with targeted viral insertion
Together, the engineered clonal controls and optimized LR-TES provide reference material and a technical framework supporting rAAV ISA in safety evaluation, particularly when high structural resolution and specificity are needed to interpret predominant integration events.
Erica Coratella, Myriam Lemmens, Mevion Oertli et al.
· Molecular Therapy: Nucleic A... · 0 citations