Open access
Jul 2026
FMR1 gene therapy restores translationally relevant phenotypes in a mouse model for fragile X syndrome.
It is shown that FMR1 gene therapy using delivery routes and vehicles approved for clinical use improves core phenotypes in a mouse model for FXS, and suggests that a dual route may be needed to achieve full brain coverage.
Richard K Lacher, Kari Henson, Lindsay N Wathen et al.
· Gene Therapy · 0 citations